3 Recruiting Angelman Syndrome Phase 3 Clinical Trials
Active phase 3 studies for angelman syndrome enrolling across the USA. Verify eligibility and contact site coordinators.
All Angelman Syndrome studiesPhase 3 Studies for Angelman Syndrome
🔵 Active, Not Recruiting Phase3
Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS)
📍 Cedars Sinai — Los Angeles, California
View Study & Checklist ➔ 🟢 Recruiting Phase3
BEACON - Phase III Clinical Study of Rugonersen in Angelman Syndrome.
📍 Rady Children's Hospital — San Diego, California
View Study & Checklist ➔ 🟢 Recruiting Phase3
REVEAL: A Phase 3 Study of Obudanersen (ION582) in Angelman Syndrome
📍 Cedars-Sinai Medical Center — Los Angeles, California
View Study & Checklist ➔