3 Recruiting Duchenne Muscular Dystrophy (DMD) Phase 1 Clinical Trials
Active phase 1 studies for duchenne muscular dystrophy (dmd) enrolling across the USA. Verify eligibility and contact site coordinators.
All Duchenne Muscular Dystrophy (DMD) studiesPhase 1 Studies for Duchenne Muscular Dystrophy (DMD)
🔵 Active, Not Recruiting Phase1 / Phase2
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping
📍 University of California San Diego — La Jolla, California
View Study & Checklist ➔ 🟡 Not Yet Recruiting Phase1 / Phase2
Glucagon-Like Peptide-1 Receptor Agonists to Attenuate Metabolic Risk in Individuals With Duchenne Muscular Dystrophy
📍 Vanderbilt University Medical Center — Nashville, Tennessee
View Study & Checklist ➔ 🟢 Recruiting Phase1
Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy
📍 Vanderbilt University Medical Center — Nashville, Tennessee
View Study & Checklist ➔