2 Recruiting Mucopolysaccharidosis I Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Recruiting Mucopolysaccharidosis I Studies
🔵 Active, Not Recruiting Phase1 / Phase2 💊 Investigational Drug / Biologic
Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I, II, and VI
📍 The Lundquist Institute at Harbor-UCLA Medical Center — Torrance, California
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Registry of Patients Diagnosed With Lysosomal Storage Diseases
📍 University of California San Francisco — San Francisco, California
View Study & Checklist ➔