7 Recruiting Pompe Disease Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Recruiting Pompe Disease Studies
🔵 Active, Not Recruiting Interventional Protocol 📊 Observational Clinical Research
Developing a Management Approach for Patients With "Late-Onset" Pompe Disease
📍 Duke University — Durham, North Carolina
View Study & Checklist ➔ 🔵 Active, Not Recruiting Phase1 / Phase2 📋 Clinical Research Protocol
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
📍 Barrow Neurological Institute — Phoenix, Arizona
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
A Global Prospective Observational Registry of Patients With Pompe Disease
📍 University of Arkansas Medical Science — Little Rock, Arkansas
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Cognitive and Neurological Pathologies in Pompe Disease
📍 Duke University Medical Center — Durham, North Carolina
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
📍 Duke University Medical Center — Durham, North Carolina
View Study & Checklist ➔ 🟢 Recruiting Phase2 💊 Investigational Drug / Biologic
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
📍 University of California - Irvine Medical Center — Irvine, California
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Avalglucosidase Alfa Pregnancy Study
📍 Investigational site worldwide — Bridgewater, New Jersey
View Study & Checklist ➔