2 Recruiting Sanfilippo Syndrome Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Recruiting Sanfilippo Syndrome Studies
🟢 Recruiting Phase2 / Phase3 💊 Investigational Drug / Biologic
An Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambroxol Hydrochloride in Adult (≥ 18 Years of Age) Subjects With MPS III
📍 Lysosomal & Rare Disorders Research & Treatment Center, Inc. — Fairfax, Virginia
View Study & Checklist ➔ 🟢 Recruiting Phase2 / Phase3 💊 Investigational Drug / Biologic
Study of Cannabidiol in Sanfilippo Syndrome
📍 The Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center — Torrance, California
View Study & Checklist ➔