Spinraza in Adult Spinal Muscular Atrophy (NCT03709784)

🧪 Interventions in This Study

• Observational study to examine safety, tolerability, and effectiveness of SPINRAZA® prescribed as part of standard of care (DRUG)

Full eligibility criteria are available on the official NIH protocol. View the criteria ↗

📍 All Participating Trial Locations (11 Sites)

• Barrow Neurological Institute — Phoenix, Arizona
• Georgetown University — Washington D.C., District of Columbia
• Johns Hopkins — Baltimore, Maryland
• Massachusetts General Hospital-Harvard University — Boston, Massachusetts
• Memorial Healthcare — Owosso, Michigan
• Washington University School of Medicine — St Louis, Missouri
• New York University School of Medicine — New York, New York
• Houston Methodist Neurological Institute — Houston, Texas
• Children's Hospital of the King's Daughthers — Norfolk, Virginia
• University of Washington — Seattle, Washington
• Montreal Neurological Institute and Hospital — Montreal, Quebec

💰 Cost, Insurance & Patient Rights

• 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
• Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
• Voluntary Participation: You may withdraw at any time without affecting your standard medical care.

More studies in Spinal Muscular Atrophy

• Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA) — Phoenix, Arizona
• Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb — Pittsburgh, Pennsylvania
• A Study to Learn About the Effect of Higher Doses of Nusinersen (BIIB058) Given as Injections to Participants With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Risdiplam (ASCEND) — Phoenix, Arizona
• Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab — Phoenix, Arizona
• Early Check: Expanded Screening in Newborns — Research Triangle Park, North Carolina

Explore by condition: All Spinal Muscular Atrophy clinical trials

💡 How to Participate

1. Check the checklist above to see if you may qualify.
2. Review the official NIH record below to find the coordinating site.
3. Ask about the visit schedule, what is covered at no cost, and any travel support.
4. Confirm with your own doctor before making a decision.