Long-term Safety and Efficacy Study of Fitusiran in Patients With Hemophilia A or B, With or Without Inhibitory Antibodies to Factor VIII or IX (NCT03754790)

🧪 Interventions in This Study

• Fitusiran (DRUG)

Full eligibility criteria are available on the official NIH protocol. View the criteria ↗

📍 All Participating Trial Locations (79 Sites)

Showing the first 25 of 79 sites.

• Phoenix Childrens Hospital Site Number : 8400009 — Phoenix, Arizona
• Children's Hospital Los Angeles Site Number : 8400019 — Los Angeles, California
• Center for Inherited Blood Disorders (CIBD) Site Number : 8400016 — Orange, California
• Nemours Children's Clinic Site Number : 8400008 — Jacksonville, Florida
• St Joseph's Children's Hospital of Tampa Site Number : 8400002 — Tampa, Florida
• Rush University Medical Center -1725 W Harrison St Site Number : 8400001 — Chicago, Illinois
• ~Massachusetts General Hospital Site Number : 8400011 — Boston, Massachusetts
• University of Michigan Hospital - 1500 E Medical Center Dr Site Number : 8400012 — Ann Arbor, Michigan
• Alliance for Childhood Diseases Site Number : 8400007 — Las Vegas, Nevada
• Childrens Hospital Medical Center of Akron Site Number : 8400006 — Akron, Ohio
• Investigational Site Number : 0360001 — Camperdown, New South Wales
• Investigational Site Number : 0360003 — Prahran, Victoria
• Investigational Site Number : 0360002 — Murdoch, Western Australia
• Investigational Site Number : 1240001 — Montreal, Quebec
• Investigational Site Number : 1560004 — Beijing,
• Investigational Site Number : 1560007 — Beijing,
• Investigational Site Number : 1560014 — Changsha,
• Investigational Site Number : 1560009 — Chengdu,
• Investigational Site Number : 1560002 — Guangzhou,
• Investigational Site Number : 1560011 — Guiyang,
• Investigational Site Number : 1560005 — Hangzhou,
• Investigational Site Number : 1560008 — Jinan,
• Investigational Site Number : 1560012 — Kunming,
• Investigational Site Number : 1560013 — Lanzhou,
• Investigational Site Number : 1560010 — Qingdao,

💰 Cost, Insurance & Patient Rights

• 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
• Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
• Voluntary Participation: You may withdraw at any time without affecting your standard medical care.

More studies in Hemophilia

• A Study to Test a Medicine (Fitusiran) Injected Under the Skin for Preventing Bleeding Episodes in Male Adolescent or Adult Participants With Severe Hemophilia — Orange, California
• Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B — Los Angeles, California
• Patient Reported Outcomes Burdens and Experiences - Phase 3 — Hamilton, Ontario
• ATHNdataset Registry — Hickory, North Carolina
• A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B — Los Angeles, California

Explore by condition: All Hemophilia clinical trials

💡 How to Participate

1. Check the checklist above to see if you may qualify.
2. Review the official NIH record below to find the coordinating site.
3. Ask about the visit schedule, what is covered at no cost, and any travel support.
4. Confirm with your own doctor before making a decision.