๐Ÿ›๏ธ Verified NIH Record โ€ข Updated 2026-07-17

HEALEY ALS Platform Trial - Master Protocol (NCT04297683)

HEALEY ALS Platform Trial

๐Ÿ”ต Active, Not Recruiting Phase2 / Phase3 ๐Ÿ’Š Investigational Drug / Biologic Sponsor: Merit E. Cudkowicz, MD

๐Ÿฉบ Plain-English Summary (8th-Grade Level)

The HEALEY ALS Platform Trial is a perpetual multi-center, multi-regimen clinical trial evaluating the safety and efficacy of investigational products for the treatment of ALS.

Who can join: Review the eligibility criteria below.

Location: Barrow Neurological Institute โ€” Phoenix, Arizona

Age range: 18 Years

๐Ÿ“‹ "Do I Qualify?" โ€” 1-Minute Self Screener

Instant Checklist

Full eligibility criteria are available on the official NIH protocol. View the criteria โ†—

๐Ÿ“ All Participating Trial Locations (81 Sites)

Showing the first 25 of 81 sites.

  • Barrow Neurological Institute โ€” Phoenix, Arizona
  • Mayo Clinic Scottsdale โ€” Scottsdale, Arizona
  • University of Arkansas for Medical Sciences โ€” Little Rock, Arkansas
  • UC San Diego โ€” La Jolla, California
  • Loma Linda University Health โ€” Loma Linda, California
  • Kaiser Permanente Los Angeles Medical Center โ€” Los Angeles, California
  • University of Southern California โ€” Los Angeles, California
  • Cedars-Sinai Medical Center โ€” Los Angeles, California
  • University of California, Irvine โ€” Orange, California
  • Forbes Norris MDA/ALS Research Center, California Pacific Medical Center โ€” San Francisco, California
  • University of California, San Francisco โ€” San Francisco, California
  • University of Colorado โ€” Aurora, Colorado
  • Hospital for Special Care โ€” New Britain, Connecticut
  • Yale University โ€” New Haven, Connecticut
  • Georgetown University โ€” Washington D.C., District of Columbia
  • George Washington University โ€” Washington D.C., District of Columbia
  • Nova Southeastern University โ€” Davie, Florida
  • University of Florida โ€” Gainesville, Florida
  • Mayo Clinic Florida โ€” Jacksonville, Florida
  • University of Miami โ€” Miami, Florida
  • University of South Florida โ€” Tampa, Florida
  • Augusta University โ€” Augusta, Georgia
  • Saint Alphonsus Regional Medical Center โ€” Boise, Idaho
  • Northwestern University โ€” Chicago, Illinois
  • University of Chicago โ€” Chicago, Illinois

๐Ÿ’ฐ Cost, Insurance & Patient Rights

  • 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
  • Routine Patient Care: Under federal law (ACA ยง 2709) and many state statutes, routine care costs are covered during participation.
  • Voluntary Participation: You may withdraw at any time without affecting your standard medical care.

๐Ÿ’ก How to Participate

  1. Check the checklist above to see if you may qualify.
  2. Review the official NIH record below to find the coordinating site.
  3. Ask about the visit schedule, what is covered at no cost, and any travel support.
  4. Confirm with your own doctor before making a decision.
๐Ÿ›๏ธ View Official NIH Record โ†—