A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria (NCT05166161)

🧪 Interventions in This Study

• PTC923 (DRUG)

Full eligibility criteria are available on the official NIH protocol. View the criteria ↗

📍 All Participating Trial Locations (46 Sites)

Showing the first 25 of 46 sites.

• Children's Hospital Colorado — Aurora, Colorado
• UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism — Gainesville, Florida
• Indiana University School of Medicine Department of Medical and Molecular Genetics — Indianapolis, Indiana
• Boston Children's Hospital — Boston, Massachusetts
• Icahn School of Medicine at Mount Sinai (ISMMS) — New York, New York
• UPMC Children's Hospital of Pittsburgh — Pittsburgh, Pennsylvania
• University of Utah — Salt Lake City, Utah
• The Queensland Children's Hospital — South Brisbane, Brisbane
• Westmead Hospital — Westmead, New South Wales
• PARC Clinical Research — Adelaide, South Australia
• Royal Children's Hospital — Parkville, Victoria
• Hospital de clinicas de Porto Alegre — Porto Alegre, Rio Grande do Sul
• Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo — Ribeirão Preto, São Paulo
• Metabolics and Genetics in Calgary (MAGIC) Clinic, Ltd. — Calgary, Alberta
• McMaster Children's Hospital Hamilton Health Sciences — Hamilton, Ontario
• The Hospital for Sick Children University of Toronto Adult Clinic: The Fred A Litwin Family Centre in Genetic Medicine University Health Network & Mt. Sinai Hospital — Toronto, Ontario
• Fakultní nemocnice Královské Vinohrady Klinika dětí a dorostu Ambulance pro léčbu PKU a HPA — Prague,
• Copenhagen University Hospital, Rigshospitalet — Copenhagen,
• Hôpital Necker-Enfants Malades - Centre de Référence des Maladies Héréditaires du Métabolisme — Paris,
• Medical Genetics and Laboratory Diagnostics Center — Tbilisi,
• University Children's Hospital Hamburg Eppendorf (Kinder-UKE) Klinik für Kinder- und Jugendmedizin (Kinder-UKE) — Hamburg,
• Universitätsklinikum Heidelberg / Zentrum für Kinder- und Jugendmedizin / Sektion für Neuropädiatrie & Stoffwechselmedizin — Heidelberg,
• Universitätsklinikum Münster — Münster,
• Azienda Ospedaliera-Universita Padova — Padua, Veneto
• Department of Human Neuroscience, Child and Adolescent Neuropsychiatry, Policlinico Umberto I — Rome,

💰 Cost, Insurance & Patient Rights

• 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
• Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
• Voluntary Participation: You may withdraw at any time without affecting your standard medical care.

More studies in Phenylketonuria

• Rapid Drug Desensitization Study in Adults Experiencing Hypersensitivity Reactions to Palynziq — Chevy Chase, Maryland
• A Phase 1/Phase 2 Open-label Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Intravenous Administration of SAR444836 in Adult Participants With Phenylketonuria — San Francisco, California
• Immune Modulation During Palynziq® Treatment in Adults (IMPALA) — Los Angeles, California
• A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria — Indianapolis, Indiana
• A Study of JNT-517 in Participants With Phenylketonuria (PKU) — Los Angeles, California

Explore by condition: All Phenylketonuria clinical trials

💡 How to Participate

1. Check the checklist above to see if you may qualify.
2. Review the official NIH record below to find the coordinating site.
3. Ask about the visit schedule, what is covered at no cost, and any travel support.
4. Confirm with your own doctor before making a decision.