🏛️ Verified NIH Record • Updated 2025-07-17
Long Term Follow-Up for Safety of AVR-RD-02 (NCT06488261)
A Long-Term Follow-Up Safety Study of Subjects With Gaucher Disease Who Previously Received AVR-RD-02
🔵 Active, Not Recruiting Interventional Protocol 📊 Observational Clinical Research Sponsor: John Bernat
🩺 Plain-English Summary (8th-Grade Level)
The goal of this observational study is to assess the safety and tolerability of AVR-RD-02 treatment in subjects who previously received AVR-RD-02 treatment (single dose administration).
Who can join: Review the eligibility criteria below.
Location: University of Iowa Hospitals and Clinics — Iowa City, Iowa
Age range: 18 Years
🧪 Interventions in This Study
📋 "Do I Qualify?" — 1-Minute Self Screener
Instant ChecklistFull eligibility criteria are available on the official NIH protocol. View the criteria ↗
📍 All Participating Trial Locations (1 Sites)
- University of Iowa Hospitals and Clinics — Iowa City, Iowa
💰 Cost, Insurance & Patient Rights
- 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
- Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
- Voluntary Participation: You may withdraw at any time without affecting your standard medical care.
More studies in Gaucher Disease
- A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED) — Durham, North Carolina
- International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry — Phoenix, Arizona
- A Long-term Follow-up Study of Gaucher Disease — Durham, North Carolina
- Gaucher Disease Outcome Survey (GOS) — Lexington, Massachusetts
- Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease — Minneapolis, Minnesota
Explore by condition: All Gaucher Disease clinical trials
💡 How to Participate
- Check the checklist above to see if you may qualify.
- Review the official NIH record below to find the coordinating site.
- Ask about the visit schedule, what is covered at no cost, and any travel support.
- Confirm with your own doctor before making a decision.