Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA) (NCT07681713)

🧪 Interventions in This Study

• Vatiquinone (DRUG)

Full eligibility criteria are available on the official NIH protocol. View the criteria ↗

📍 All Participating Trial Locations (9 Sites)

• University of California Los Angeles — Los Angeles, California
• University of South Florida — Tampa, Florida
• University of Iowa — Iowa City, Iowa
• Children's Hospital of Philadelphia — Philadelphia, Pennsylvania
• Hôpital Érasme (Hôpital Universitaire de Bruxelles) — Brussels,
• University of Campinas — Campinas, São Paulo
• Centre Hospitalier de l'Universite de Montreal CHUM — Montreal, Quebec
• Institut du Cerveau et de la Moelle Epinière — Paris,
• Hospital Sant Joan de Deu — Barcelona,

📞 Contact the Study Coordinator

Phone: (866) 562-4620

Email: medinfo@ptcbio.com

Coordinator details come directly from the registered NIH protocol. Confirm the study is still recruiting before traveling.

💰 Cost, Insurance & Patient Rights

• 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
• Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
• Voluntary Participation: You may withdraw at any time without affecting your standard medical care.

More studies in Friedreich's Ataxia

• Characterization of the Cardiac Phenotype of Friedreich's Ataxia (FRDA) — New York, New York
• Biomarkers in Friedreich's Ataxia — Gainesville, Florida

Explore by condition: All Friedreich's Ataxia clinical trials

💡 How to Participate

1. Check the checklist above to see if you may qualify.
2. Contact the study coordinator using the phone/email above.
3. Ask about the visit schedule, what is covered at no cost, and any travel support.
4. Confirm with your own doctor before making a decision.