Study of LX2006 Gene Therapy in Friedreich Ataxia Cardiomyopathy (NCT07721025)
A Phase 2, Multicenter, Open-label, Randomized, Controlled Study of LX2006 Gene Therapy in Participants With Friedreich Ataxia Cardiomyopathy (SUNRISE-FA 2)
🩺 Plain-English Summary (8th-Grade Level)
The purpose of Study LX2006-03, a multicenter, Phase 2, open-label, randomized, controlled study, is to evaluate the efficacy and safety of LX2006 gene therapy in participants with Friedreich ataxia (FA) cardiomyopathy (CM).
Who can join: Review the eligibility criteria below.
Location: University of South Florida — Tampa, Florida
Age range: 6 Years
🧪 Interventions in This Study
- LX2006 (GENETIC)
- Usual Care (OTHER)
📋 "Do I Qualify?" — 1-Minute Self Screener
Instant ChecklistFull eligibility criteria are available on the official NIH protocol. View the criteria ↗
📍 All Participating Trial Locations (1 Sites)
- University of South Florida — Tampa, Florida
📞 Contact the Study Coordinator
Phone: (212) 547-9879
Email: clinicaltrials@lexeotx.com
Coordinator details come directly from the registered NIH protocol. Confirm the study is still recruiting before traveling.
💰 Cost, Insurance & Patient Rights
- 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
- Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
- Voluntary Participation: You may withdraw at any time without affecting your standard medical care.
More studies in Friedreich Ataxia
- A Study to Find Out How BIIB141 (Omaveloxolone) is Processed in the Body and to Learn More About Its Safety in Participants With Friedreich's Ataxia Aged 2 to 15 Years Old — Philadelphia, Pennsylvania
- A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA) — Gainesville, Florida
- FA Clinical Outcome Measures — Los Angeles, California
- A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia — Los Angeles, California
- Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia — Los Angeles, California
- Clinical Course Of Disease In Participants With FA-CM — La Jolla, California
Explore by condition: All Friedreich Ataxia clinical trials
💡 How to Participate
- Check the checklist above to see if you may qualify.
- Contact the study coordinator using the phone/email above.
- Ask about the visit schedule, what is covered at no cost, and any travel support.
- Confirm with your own doctor before making a decision.