16 Recruiting Paroxysmal Nocturnal Hemoglobinuria Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Interventions for Paroxysmal Nocturnal Hemoglobinuria
Top Recruiting Paroxysmal Nocturnal Hemoglobinuria Studies
Assess Long-Term Safety of Danicopan Add-on Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria: Analysis of IPIG-Registry Data
📍 Clinical Research Site — Boston, Massachusetts
View Study & Checklist ➔A Study Evaluating the Efficacy and Safety of Crovalimab Versus Eculizumab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Not Previously Treated With Complement Inhibitors
📍 Organizacion Medica de Investigacion (OMI) — Ciudad Autonoma Buenos Aires,
View Study & Checklist ➔Long-term Safety of Danicopan: IPIG Registry-based Cohort Study
📍 Alexion Pharmaceuticals, Inc. (Sponsor) — Boston, Massachusetts
View Study & Checklist ➔A Long-term Safety and Efficacy Study of Danicopan as an Add-on Therapy to Complement Component 5 Inhibitor (C5i) in Participants With PNH
📍 Research Site — Los Angeles, California
View Study & Checklist ➔Long-term Safety and Tolerability of Iptacopan in Patients With Paroxysmal Nocturnal Hemoglobinuria
📍 City Of Hope National Med Center — Duarte, California
View Study & Checklist ➔A Study to Evaluate How Safe Pozelimab + Cemdisiran Combination Therapy is and How Well it Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Have Not Recently Received or Have Not Received Complement Inhibitor Treatment
📍 The Oncology Institute of Hope & Innovation — Whittier, California
View Study & Checklist ➔A Study Evaluating the Safety, Pharmacokinetics, and Efficacy of Crovalimab Versus Eculizumab in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Currently Treated With Complement Inhibitors
📍 Carolinas Healthcare System — Charlotte, North Carolina
View Study & Checklist ➔Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis
📍 Research Site — Saskatoon, Saskatchewan
View Study & Checklist ➔The International PNH Interest Group PNH Registry
📍 International PNH Interest Group — Altamonte Springs, Florida
View Study & Checklist ➔A Study to Evaluate How Pozelimab + Cemdisiran Combination Therapy Works in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Whose Current Treatment is Not Working Efficiently
📍 Hospital das Clinicas da FMRP USP — Ribeirão Preto, São Paulo
View Study & Checklist ➔A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
📍 Liverpool Hospital — Liverpool, New South Wales
View Study & Checklist ➔Global PNH Patient Registry
📍 Aplastic Anemia and MDS International Foundation — Bethesda, Maryland
View Study & Checklist ➔Home Reported Outcomes in PNH
📍 Novartis Investigative Site — East Hanover, New Jersey
View Study & Checklist ➔A Study in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) to Evaluate How Safe Long-term Treatment With Pozelimab + Cemdisiran Combination Therapy is and How Well it Works
📍 Toronto General Hospital — Toronto, Ontario
View Study & Checklist ➔