4 Recruiting Spinal Muscular Atrophy Interventional Protocol Clinical Trials
Active interventional protocol studies for spinal muscular atrophy enrolling across the USA. Verify eligibility and contact site coordinators.
All Spinal Muscular Atrophy studiesInterventional Protocol Studies for Spinal Muscular Atrophy
🔵 Active, Not Recruiting Interventional Protocol
Spinraza in Adult Spinal Muscular Atrophy
📍 Barrow Neurological Institute — Phoenix, Arizona
View Study & Checklist ➔ 🔵 Active, Not Recruiting Interventional Protocol
Early Check: Expanded Screening in Newborns
📍 RTI International — Research Triangle Park, North Carolina
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol
Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
📍 St. Jude Children's Research Hospital — Memphis, Tennessee
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol
Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
📍 Columbia University Irving Medical Center — New York, New York
View Study & Checklist ➔