4 Recruiting Wilson Disease Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Recruiting Wilson Disease Studies
🔵 Active, Not Recruiting Interventional Protocol 📊 Observational Clinical Research
Prescreening Study to Identify Potential Wilson Disease Participants for Gene-Editing Clinical Trial
📍 University of California Los Angeles Medical Center — Los Angeles, California
View Study & Checklist ➔ 🔵 Active, Not Recruiting Phase1 / Phase2 💊 Investigational Drug / Biologic
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease
📍 University of California Los Angeles — Los Angeles, California
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Natural History of Wilson Disease
📍 Yale University — New Haven, Connecticut
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Off Treatment Urinary Copper Excretion in Wilson Disease, Pilot Study
📍 Yale School of Medicine — New Haven, Connecticut
View Study & Checklist ➔