🏛️ Verified NIH Record • Updated 2026-05-11
Prescreening Study to Identify Potential Wilson Disease Participants for Gene-Editing Clinical Trial (NCT07226622)
Prescreening Study to Identify Potential Participants for a Clinical Study in Wilson Disease (WD) Due to the ATP7B p.H1069Q or p.R778L Mutations
🔵 Active, Not Recruiting Interventional Protocol 📊 Observational Clinical Research Sponsor: Prime Medicine, Inc.
🩺 Plain-English Summary (8th-Grade Level)
The aim of this study is to inform and improve future clinical trials in Wilson Disease (WD) by better understanding how patients with WD are living with and managing the disease, and by identifying key factors that shape their decisions to participate in clinical research.
Who can join: Review the eligibility criteria below.
Location: University of California Los Angeles Medical Center — Los Angeles, California
Age range: 18 Years
📋 "Do I Qualify?" — 1-Minute Self Screener
Instant ChecklistFull eligibility criteria are available on the official NIH protocol. View the criteria ↗
📍 All Participating Trial Locations (7 Sites)
- University of California Los Angeles Medical Center — Los Angeles, California
- University of California Davis Health — Sacramento, California
- Yale New Haven Hospital — New Haven, Connecticut
- Northwestern University — Chicago, Illinois
- Massachusetts General Hospital — Boston, Massachusetts
- University of Michigan Medicine — Ann Arbor, Michigan
- American Research Corporation — San Antonio, Texas
💰 Cost, Insurance & Patient Rights
- 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
- Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
- Voluntary Participation: You may withdraw at any time without affecting your standard medical care.
More studies in Wilson Disease
- A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease — Los Angeles, California
- Natural History of Wilson Disease — New Haven, Connecticut
- Off Treatment Urinary Copper Excretion in Wilson Disease, Pilot Study — New Haven, Connecticut
Explore by condition: All Wilson Disease clinical trials
💡 How to Participate
- Check the checklist above to see if you may qualify.
- Review the official NIH record below to find the coordinating site.
- Ask about the visit schedule, what is covered at no cost, and any travel support.
- Confirm with your own doctor before making a decision.