Advancing Integrated Therapies for Gaucher Disease (NCT07758816)
Advancing Integrated Therapies for Gaucher Disease: Neuronopathic Innovation and Combination Strategies for Refractory Skeletal Disease
🩺 Plain-English Summary (8th-Grade Level)
The purpose of this study is to better understand the natural history, clinical outcomes, and biological features of Gaucher disease in patients receiving standard medical care
Who can join: Review the eligibility criteria below.
Location: Yale New Haven Health System — New Haven, Connecticut
Age range: 3 Months to 75 Years
📋 "Do I Qualify?" — 1-Minute Self Screener
Instant ChecklistFull eligibility criteria are available on the official NIH protocol. View the criteria ↗
📍 All Participating Trial Locations (1 Sites)
- Yale New Haven Health System — New Haven, Connecticut
📞 Contact the Study Coordinator
Phone: (203) 785-3412
Email: Ruhua.Yang@yale.edu
Coordinator details come directly from the registered NIH protocol. Confirm the study is still recruiting before traveling.
💰 Cost, Insurance & Patient Rights
- 100% Free Items: The investigational treatment and protocol-required procedures are supplied at zero cost by the sponsor.
- Routine Patient Care: Under federal law (ACA § 2709) and many state statutes, routine care costs are covered during participation.
- Voluntary Participation: You may withdraw at any time without affecting your standard medical care.
More studies in Gaucher Disease
- A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED) — Durham, North Carolina
- Long Term Follow-Up for Safety of AVR-RD-02 — Iowa City, Iowa
- International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry — Phoenix, Arizona
- A Long-term Follow-up Study of Gaucher Disease — Durham, North Carolina
- Gaucher Disease Outcome Survey (GOS) — Lexington, Massachusetts
- Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease — Minneapolis, Minnesota
Explore by condition: All Gaucher Disease clinical trials
💡 How to Participate
- Check the checklist above to see if you may qualify.
- Contact the study coordinator using the phone/email above.
- Ask about the visit schedule, what is covered at no cost, and any travel support.
- Confirm with your own doctor before making a decision.